After two years of treatment with Elevidys, we are seeing multiple sustained benefits in the day-to-day lives of these young boys, all of which are indicators of its disease modifying potential in Duchenne,” said Levi Garraway, M.D., Ph.D., Roche’s Chief Medical Officer and Head of Global Product Development.

Partnership expands Integrated Biosciences’ partnerships in translational research and Project 8p Foundation’s footprint in therapeutic development

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Their patient-led consortium is creating a free and open database for

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Team IMPACT is a national non-profit organization, has developed a unique multi-year program that matches children facing serious illnesses and…

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Source Article The Rare As One Project, supports 30 patient-led rare disease organizations that are working to develop and strengthen a collaborative research network in…