What is a “Rare Disease”?
In the United States, a rare disease affects 200,000 or fewer persons
Globally, 350 Million people suffer from a rare disease. This is greater than the entire population of the U.S.
Number of Rare Diseases: 7000+
Examples include: Amyotrophic Lateral Sclerosis (ALS), Duchenne Muscular Dystrophy, Cystic Fibrosis, All Childhood Cancers